Status | Study |
Completed |
Study Name: MND-ADA Transduction of CD34+ Cells From Children With ADA-SCID Condition: Severe Combined Immunodeficiency Date: 2008-11-19 Interventions: Biological: ADA gene transfer Autologous CD34+ cells transduced with the retroviral vector MND-ADA, carr |
Active, not recruiting |
Study Name: ADA Gene Transfer Into Hematopoietic Stem/Progenitor Cells for the Treatment of ADA-SCID Condition: Immunologic Deficiency Syndromes Date: 2008-01-10 Interventions: Genetic: Gene transduced CD34+ cells infusion of autologous CD34+ cells transduced with retroviral vecto |
Completed |
Study Name: Gene Therapy for ADA-SCID Condition: Severe Combined Immunodeficiency Syndrome Date: 2008-01-08 Interventions: Genetic: gene transduced PBL and/or gene transduced HSC infusions of autologous PBL and/or HSC transduce |
No longer available |
Study Name: Emergency Use of Adoptive Immunotherapy With CMV-Specific T Cells After Donor Bone Marrow Transplant of an Infant With Immunodeficiency Syndrome and CMV Infection Condition: Infection Precancerous/Nonmalignant Condition Date: 2007-10-19 Interventions: Biological: therapeutic allogeneic lymphocytes |
Recruiting |
Study Name: The Role of Bacteria and Genetic Variations in Cystic Fibrosis Condition: Lung Diseases Date: 2006-07-13 |
Completed |
Study Name: Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency Condition: Severe Combined Immunodeficiency Syndrome Date: 2001-06-27 Interventions: Drug: CD34+ cells transduced with ADA retrovir |
Enrolling by invitation |
Study Name: Molecular and Clinical Studies of Primary Immunodeficiency Diseases Condition: Immunologic Deficiency Syndrome Date: 2000-09-30 |
Completed |
Study Name: Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency: A Natural History Study Condition: Severe Combined Immunodeficiency Date: 1999-11-03 Interventions: Drug: ADA PBSC Drug: ADA Umbilical Cord Bl |